Geneva, March 23 -- International Clinical Trials Registry received information related to the study (NCT07471516) titled 'Zoledronic Acid Treatment in Patients With Congenital Dyserythropoietic Anemia' on March 3.
Study Type: Interventional
Study Design:
Allocation: N/A. Intervention model: Single Group Assignment. Primary purpose: Treatment. Masking: None (Open Label).
Primary Sponsor: Institute of Hematology & Blood Diseases Hospital, China
Condition:
Congenital Dyserythropoietic Anemia (CDA)
Intervention:
Drug: zoledronic acid
Recruitment Status: Recruiting
Phase: Phase 1/Phase 2
Date of First Enrollment: February 25, 2026
Target Sample Size: 2
Countries of Recruitment:
China
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