Geneva, Oct. 9 -- International Clinical Trials Registry received information related to the study (NCT07855562) titled 'MPS IIIA Disease Monitoring Program' on Sept. 25.
Study Type: Observational
Primary Sponsor: Ultragenyx Pharmaceutical Inc
Condition:
MPS IIIA
Sanfilippo Syndrome
Sanfilippo A
Mucopolysaccharidosis III
Intervention:
Other: No Intervention
Recruitment Status: Not recruiting
Date of First Enrollment: November 2026
Target Sample Size: 55
To know more, visit https://clinicaltrials.gov/study/NCT07855562
Disclaimer: Curated by HT Syndication....