Clinical Trial: A Study of Risdiplam in Participants With Type I and Type II Spinal Muscle Atrophy (SMA)

U.S., April 16 -- ClinicalTrials.gov registry received information related to the study (NCT07531719) titled 'A Study of Risdiplam in Participants With Type I and Type II Spinal Muscle Atrophy (SMA)' on April 08.

Brief Summary: This multicenter, non-interventional, prospective study with a retrospective component aims to evaluate the real-world clinical outcomes, safety profile, and motor function improvements of Risdiplam treatment in participants with Type I and Type II Spinal Muscle Atrophy over 24 months of treatment.

The study will allow retrospective collection of medical history data and previous participants visits from the medical records.

Study Start Date: April 15

Study Type: OBSERVATIONAL

Condition: Spinal Muscle Atrophy ...