U.S., May 14 -- ClinicalTrials.gov registry received information related to the study (NCT07585136) titled 'Stem Cell Mobilization and Apheresis for Life-threatening Blood Disorders' on April 16.
Brief Summary: The purpose of this study is to investigate mobilization and collection of HSPCs in patients with bone marrow failure syndromes (BMFS) using granulocyte-colony stimulating factor (otherwise known as Filgrastim) with plerixafor to demonstrate safety and feasibility of collecting HSPCs to advance gene therapy.
Primary objective:
- To characterize the safety of Filgrastim plus plerixafor in participants with bone marrow failure syndromes as determined by the incidence of adverse events (AEs).
Secondary Objectives:
* To characterize...