U.S., July 30 -- ClinicalTrials.gov registry received information related to the study (NCT07734090) titled 'Natural History of MADD' on July 24.
Brief Summary: The objective of this study is to conduct a longitudinal, observational investigation to determine the natural history of Multiple Acyl-CoA Dehydrogenase Deficiency (MADD), delineate the spectrum of its clinical features and their progression, identify biomarkers, and develop and validate patient reported outcomes.
Study Start Date: July, 2026
Study Type: OBSERVATIONAL
Condition:
Multiple Acyl-CoA Dehydrogenase Deficiency
Recruitment Status: NOT_YET_RECRUITING
Sponsor: Icahn School of Medicine at Mount Sinai
Information provided by (Responsible Party): Mary LoPiccolo, Icahn ...