Tokyo, June 13 -- UMIN Clinical Trials Registry (UMIN-CTR) received information related to the study (UMIN000061891) titled 'A multicenter observational study for the higher dose regimen of Nusinersen' on June 12.
Study Type:
Observational
Primary Sponsor:
Institute - Kagoshima University Graduate School of Medical and Dental Sciences
Condition:
Condition - Participants with later-onset 5q spinal muscular atrophy (SMA)
Classification by malignancy - Others
Genomic information - YES
Objective:
Narrative objectives1 - To evaluate the therapeutic effects of higher dose nusinersen on patient-reported health status and physical function in individuals with later-onset SMA
Basic objectives2 - Others
Eligibility:
Age-lower limit - 18
years-o...