US Patent Issued to University of Massachusetts on June 9 for "Methods and compositions for treating GM1 gangliosidosis" (Massachusetts Inventors)

ALEXANDRIA, Va., June 9 -- United States Patent no. 12,648,978, issued on June 9, was assigned to University of Massachusetts (Westborough, Mass.).

"Methods and compositions for treating GM1 gangliosidosis" was invented by Miguel Sena-Esteves (Westford, Mass.), Cara Weismann (Worcester, Mass.), Diane Golebiowski (Lexington, Mass.) and Lorelei Stoica (Worcester, Mass.).

According to the abstract* released by the U.S. Patent & Trademark Office: "Aspects of the invention relate to recombinant adeno-associated viruses (rAAVs). In some aspects, the rAAVs comprise artificial genetic regulatory elements that modulate transgene expression. In some aspects, the disclosure relates to the treatment of lysosomal storage disorders."

The patent was fi...