US Patent Issued to The Regents of the University of California on Sept. 1 for "Methods of treating mitochondrial disorders" (California Inventor)

ALEXANDRIA, Va., Sept. 1 -- United States Patent no. 12,723,062, issued on Sept. 1, was assigned to The Regents of the University of California (Oakland, Calif.).

"Methods of treating mitochondrial disorders" was invented by Stephanie Cherqui (La Jolla, Calif.).

According to the abstract* released by the U.S. Patent & Trademark Office: "Provided herein are methods for treating a disease or disorder associated with mitochondrial dysfunction through ex vivo introduction of a nucleic acid molecule into hematopoietic stem and progenitor cells (HSPCs) followed by transplantation of the HSPCs into a subject in need of treatment. The nucleic acid molecule may include a functional human frataxin (hFXN) or may include a gene editing system that wh...