US Patent Issued to The Board of Trustees of the Leland Stanford Junior University on Sept. 15 for "Targeting the human CCR5 locus as a safe harbor for the expression of therapeutic proteins" (California Inventors)

ALEXANDRIA, Va., Sept. 15 -- United States Patent no. 12,735,711, issued on Sept. 15, was assigned to The Board of Trustees of the Leland Stanford Junior University (Stanford, Calif.).

"Targeting the human CCR5 locus as a safe harbor for the expression of therapeutic proteins" was invented by Natalia Gomez-Ospina (Stanford, Calif.), Matthew H. Porteus (Stanford, Calif.), Samantha Glynne Scharenberg (Stanford, Calif.) and Alvaro Amorin (Stanford, Calif.).

According to the abstract* released by the U.S. Patent & Trademark Office: "The present disclosure provides methods and compositions for treating lysosomal storage disorders in subjects, comprising genetically modifying cells from the subjects ex vivo by integrating therapeutic transgenes...