ALEXANDRIA, Va., July 16 -- United States Patent no. 12,359,202, issued on July 15, was assigned to AVIDITY BIOSCIENCES INC. (San Diego).
"Anti-transferrin receptor antibody-PMO conjugates for inducing DMD exon 44 skipping" was invented by Beatrice Diana Darimont (San Diego), Usue Etxaniz Irigoien (San Diego), Venkata Ramana Doppalapudi (San Diego), Michael Caramian Cochran (La Jolla, Calif.), Isaac Marks (San Diego) and Tyler Albin (San Diego).
According to the abstract* released by the U.S. Patent & Trademark Office: "Disclosed herein are antibody oligonucleotide conjugates and pharmaceutical compositions that induce an alteration in an incorrectly spliced dystrophin mRNA transcript to induce exon 44 skipping. Also described herein incl...