Geneva, April 27 -- International Clinical Trials Registry received information related to the study (NCT07536269) titled 'Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Crinecerfont in Participants With Classic Congenital Adrenal Hyperplasia (CAH) Who Are Less Than 4 Years Old' on April 10.
Study Type: Interventional
Study Design:
Allocation: N/A. Intervention model: Single Group Assignment. Primary purpose: Treatment. Masking: None (Open Label).
Primary Sponsor: Neurocrine Biosciences
Condition:
Congenital Adrenal Hyperplasia
Intervention:
Drug: Crinecerfont
Recruitment Status: Not recruiting
Phase: Phase 2
Date of First Enrollment: April 2026
Target Sample Size: 20
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