U.S., June 6 -- ClinicalTrials.gov registry received information related to the study (NCT07630389) titled 'Remote Assessments and Genetic Determinants of Congenital and Childhood Myotonic Dystrophy' on June 01.
Brief Summary: Myotonic dystrophy type 1 (DM1) can affect people in many different ways, even in the same family. The symptoms that children experience can be different and more severe than adults. Prior studies in children have been limited because only a small number of children could participate. In this study, we hope to learn more about these differences and what causes them.
This is an observational study conducted in participants' homes and does not require travel. Instead, we will use video calls to talk with children and ...