Geneva, Jan. 12 -- International Clinical Trials Registry received information related to the study (NCT07313618) titled 'Safety and Efficacy of a Single Suprachoroidal Injection of JWK010 Gene Therapy in Subjects With Oculocutaneous Albinism Type 1 (OCA1)' on Dec. 17, 2025.
Study Type: Interventional
Study Design:
Allocation: Non-Randomized. Intervention model: Sequential Assignment. Primary purpose: Treatment. Masking: Single (Participant).
Primary Sponsor: West China Hospital
Condition:
Oculocutaneous Albinism (OCA)
Intervention:
Genetic: JWK010 gene therapy
Recruitment Status: Recruiting
Phase: Early Phase 1
Date of First Enrollment: December 22, 2025
Target Sample Size: 18
Countries of Recruitment:
China
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