U.S., May 2 -- ClinicalTrials.gov registry received information related to the study (NCT07560956) titled 'Quality of Life in Untreated Fabry' on April 24.
Brief Summary: Fabry disease is a rare, inherited condition that can affect multiple organs, including the heart, kidneys, and nervous system. Many people with Fabry disease live for a period of time without receiving disease-specific treatment, for example because treatment criteria have not yet been met. There is limited knowledge about how patients experience this period without treatment.
The purpose of this study is to improve understanding of how adults with Fabry disease who are not yet receiving disease-specific treatment experience their quality of life, their daily lives, and...