Clinical Trial: Evaluating the Safety and Effects of AMP-101 in People With DOK7 Congenital Myasthenia Syndrome

U.S., Sept. 22 -- ClinicalTrials.gov registry received information related to the study (NCT07830563) titled 'Evaluating the Safety and Effects of AMP-101 in People With DOK7 Congenital Myasthenia Syndrome' on Sept. 15.

Brief Summary: This study is evaluating the safety and potential effects of AMP-101 in people with DOK7 Congenital Myasthenia Syndrome (CMS). Participants will receive a single dose of the study treatment and will be monitored to assess their health and response to treatment. Approximately 4 participants are expected to take part in the study.

Study Start Date: Oct. 01

Study Type: INTERVENTIONAL

Condition: Congenital Myasthenia Syndrome

Intervention: DRUG: AMP-101

Route of Administration: intravenous infusion Unit Do...