Clinical Trial: A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With α- or β-Non-Transfusion-Dependent Thalassemia

U.S., April 9 -- ClinicalTrials.gov registry received information related to the study (NCT07517133) titled 'A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With α- or β-Non-Transfusion-Dependent Thalassemia' on March 26.

Brief Summary: The primary objective of this study is to compare the effect of mitapivat versus placebo on anemia in pediatric participants with alpha- or beta-non-transfusion-dependent thalassemia.

Study Start Date: Sept., 2026

Study Type: INTERVENTIONAL

Condition: Non-Transfusion-dependent Alpha-Thalassemia Non-Transfusion-dependent Beta-Thalassemia

Intervention: DRUG: Mitapivat

Tablets or Granules

DRUG: Placebo Matching Mitapivat

Tablets or Gra...