Clinical Trial: A Real-World Medical Chart Review of Spinal Muscular Atrophy Patients Treated With Onasemnogene Abeparvovec in Saudi Arabia

U.S., July 31 -- ClinicalTrials.gov registry received information related to the study (NCT07737756) titled 'A Real-World Medical Chart Review of Spinal Muscular Atrophy Patients Treated With Onasemnogene Abeparvovec in Saudi Arabia' on July 27.

Brief Summary: The aim of this retrospective medical chart review is to describe the clinical outcomes, clinical characteristics, and demographics of patients with spinal muscular atrophy (SMA) type 1 treated with onasemnogene abeparvovec (OA) at a single clinical center in Saudi Arabia. The study will use secondary data collected from the electronic medical records of SMA type 1 patients.

Study Start Date: Aug. 20

Study Type: OBSERVATIONAL

Condition: Spinal Muscular Atrophy

Recruitment Status...