Clinical Trial: WiTNNess - TNNT1 Myopathy Natural History Study

U.S., April 19 -- ClinicalTrials.gov registry received information related to the study (NCT06374719) titled 'WiTNNess - TNNT1 Myopathy Natural History Study' on April 12.

Brief Summary: WiTNNess is designed to accurately document the natural course and variation of muscle disease caused by pathogenic changes of the TNNT1 gene. The primary aim of the study is to specify meaningful outcome measures for future clinical trials. WiTNNess is open to children and adults worldwide. Participants can choose to include their information once (cross-sectional cohort) or every few months (prospective cohort).

Study Type: Observational [Patient Registry]

Condition: * TNNT1-associated Myopathy

* Infantile-onset Nemaline Rod Myopathy

* Myopathies, Ne...